Muscular Dystrophy News Today covered the latest studies, treatment advances, and clinical trials for different types of the ...

How can you measure a person's quality of life? For columnist Patrick Moeschen, the key is deciding for yourself what a good ...

Background noise and multiple conversations are a few issues that cause columnist Robin Stemple to have difficulty hearing, despite his aids.

Learning that three of her sons had DMD challenged columnist Betty Vertin, but now she embraces the highs and lows of the experience.

Arrakis Therapeutics’ investigational RNA-targeted small molecule (rSM) therapies were found to work as intended in preclinical studies and eased symptoms in a mouse model of myotonic dystrophy type 1 ...

Agamree (vamorolone) has been recommended for use in the National Health Service (NHS) in England, Wales, and Northern Ireland for treating Duchenne muscular dystrophy (DMD) patients, 4 and older. “We ...

The investigational oral therapy sevasemten significantly reduced markers of muscle damage in people with Becker muscular dystrophy (BMD) treated in a Phase 2 trial, according to top-line results ...

Living with Duchenne muscular dystrophy (DMD) has involved a series of challenges and triumphs, each shaping the person I am today. As 2025 approaches, I’m reflecting on that journey as well as ...