Nearly 4 of every 5 infants with spinal muscular atrophy (SMA) type 1 born in Italy during the era of disease-modifying therapies (DMTs) are still alive, illustrating that such treatment has ...
Natalie Katz, MD, is an assistant professor of pediatrics in the division of neurology at Duke University and co-directs the Duke Children’s Neuromuscular Program, which provides comprehensive ...